Saving Eliza: Gene Therapy Offers New Hope for Girl With Childhood Alzheimer’s

Aug 17, 2016 at 4:46 pm |

Eliza is doing better than predicted

Eliza O’Neill was born a happy child, but her parents started noticing something strange and took her to the doctor. She was diagnosed with a degenerative gene disorder that her parents learned would slowly shut off her body until her teenage years when she would most likely die. Near the end of her life, she wouldn’t be able to eat, speak, breathe or see. She would be a vegetable for most of her very short life. But this fate was too horrible to stomach, and the O’Neill’s worked as hard as they could to save her from a long, painful death. Now, there’s hope for Eliza and other children with Sanfilippo.

eliza o'neill gene therapy recipient sanfilippo

Source: YouTube @VonWong

Eliza O’Neill was fated to slowly deteriorate and die when she was just in her teens, but an experimental treatment is giving her a new life.

Eliza is already living a more fruitful life